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OpenAlex Citation Counts

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OpenAlex is a bibliographic catalogue of scientific papers, authors and institutions accessible in open access mode, named after the Library of Alexandria. It's citation coverage is excellent and I hope you will find utility in this listing of citing articles!

If you click the article title, you'll navigate to the article, as listed in CrossRef. If you click the Open Access links, you'll navigate to the "best Open Access location". Clicking the citation count will open this listing for that article. Lastly at the bottom of the page, you'll find basic pagination options.

Requested Article:

Intrathecal AAV9/AP4M1 gene therapy for hereditary spastic paraplegia 50 shows safety and efficacy in preclinical studies
Xin Chen, Thomas Dong, Yuhui Hu, et al.
Journal of Clinical Investigation (2023) Vol. 133, Iss. 10
Open Access | Times Cited: 26

Showing 1-25 of 26 citing articles:

AAV gene therapy for hereditary spastic paraplegia type 50: a phase 1 trial in a single patient
James J. Dowling, Terry Pirovolakis, Keshini Devakandan, et al.
Nature Medicine (2024) Vol. 30, Iss. 7, pp. 1882-1887
Open Access | Times Cited: 10
IMPC impact on preclinical mouse models
Sabine M. Hölter, Pilar Cacheiro, Damian Smedley, et al.
Mammalian Genome (2025)
Open Access
Preclinical use of a clinically-relevant scAAV9/SUMF1 vector for the treatment of multiple sulfatase deficiency
Maximiliano Presa, Rachel M. Bailey, Somdatta Ray, et al.
Communications Medicine (2025) Vol. 5, Iss. 1
Open Access
Focused ultrasound widely broadens AAV-delivered Cas9 distribution and activity
Emrah Gumusgoz, Sahba Kasiri, Ibrahim Youssef, et al.
Gene Therapy (2025)
Closed Access
Riboflavin transporter deficiency: AAV9-SLC52A2 gene therapy as a new therapeutic strategy
Chugang Mei, Valentina Magliocca, Xin Chen, et al.
Frontiers in Cellular Neuroscience (2025) Vol. 19
Open Access
Genetic editing of primary human dorsal root ganglion neurons using CRISPR-Cas9
Seph M. Palomino, Katherin Gabriel, Juliet M. Mwirigi, et al.
Scientific Reports (2025) Vol. 15, Iss. 1
Open Access
Emerging therapies for childhood-onset movement disorders
Lindsey Vogt, Vicente Quiroz, Darius Ebrahimi‐Fakhari
Current Opinion in Pediatrics (2024) Vol. 36, Iss. 3, pp. 331-341
Closed Access | Times Cited: 3
Plasma Neurofilament Light Chain Is Elevated in Adaptor Protein Complex 4‐Related Hereditary Spastic Paraplegia
Julian E. Alecu, Afshin Saffari, M. L. ZIEGLER, et al.
Movement Disorders (2023) Vol. 38, Iss. 9, pp. 1742-1750
Open Access | Times Cited: 7
Scientific and Regulatory Policy Committee Technical Review: Biology and Pathology of Ganglia in Animal Species Used for Nonclinical Safety Testing
Bindu Bennet, Ingrid D. Pardo, Basel T. Assaf, et al.
Toxicologic Pathology (2023) Vol. 51, Iss. 5, pp. 278-305
Closed Access | Times Cited: 7
Neddylation of protein, a new strategy of protein post-translational modification for targeted treatment of central nervous system diseases
Qian Wu, Ziang Geng, Lu Jun, et al.
Frontiers in Neuroscience (2024) Vol. 18
Open Access | Times Cited: 2
Preclinical alternative drug discovery programs for monogenic rare diseases. The case of hereditary spastic paraplegias
Matteo Rossi Sebastiano, Shinji Hadano, Fabrizia Cesca, et al.
Drug Discovery Today (2024) Vol. 29, Iss. 10, pp. 104138-104138
Open Access | Times Cited: 2
Genetic editing of primary human dorsal root ganglion neurons using CRISPR-Cas9 with functional confirmation
Seph M. Palomino, Katherin Gabriel, Juliet M. Mwirigi, et al.
bioRxiv (Cold Spring Harbor Laboratory) (2024)
Open Access | Times Cited: 1
CRISPR/Cas9-mediated neuronal deletion of 5-lipoxygenase alleviates deficits in mouse models of epilepsy
Qi-Wen Guan, Zhaojun Wang, Kai Zhang, et al.
Journal of Advanced Research (2024) Vol. 63, pp. 73-90
Open Access | Times Cited: 1
Expression and distribution of rAAV9 intrathecally administered in juvenile to adolescent mice
Irvin T. Garza, M. Eller, Sydni K. Holmes, et al.
Gene Therapy (2024)
Open Access | Times Cited: 1
AAV9/SLC6A1 gene therapy rescues abnormal EEG patterns and cognitive behavioral deficiencies in Slc6a1-/- mice
Weirui Guo, Matthew Rioux, Frances C. Shaffo, et al.
Journal of Clinical Investigation (2024) Vol. 135, Iss. 3
Open Access | Times Cited: 1
Neuropathological Findings in Nonclinical Species Following Administration of Adeno-Associated Virus (AAV)-Based Gene Therapy Vectors
Brad Bolon, Elizabeth L. Buza, Elizabeth J. Galbreath, et al.
Toxicologic Pathology (2024)
Closed Access | Times Cited: 1
Restoring adapter protein complex 4 function with small molecules: an in silico approach to spastic paraplegia 50
San Francisco, Lorenzo Lamacchia, Alberto Turco, et al.
Protein Science (2024) Vol. 34, Iss. 1
Open Access | Times Cited: 1
Paving a way to treat spastic paraplegia 50
Jonathan R. Brent, Han‐Xiang Deng
Journal of Clinical Investigation (2023) Vol. 133, Iss. 10
Open Access | Times Cited: 2
Hereditäre spastische Spinalparalysen erkennen und behandeln
Sven Klimpe
NeuroTransmitter (2024) Vol. 35, Iss. 7-8, pp. 36-41
Closed Access
Sbno1 mediates cell–cell communication between neural stem cells and microglia through small extracellular vesicles
Yifan Zhang, Zhihan Zhu, Zhinuo Li, et al.
Cell & Bioscience (2024) Vol. 14, Iss. 1
Open Access
Adeno-associated virus-mediated gene therapy in central nervous system genetic disorders
Qinglan Ling, Andrea Boitnott, Irvin T. Garza, et al.
Elsevier eBooks (2024), pp. 155-172
Closed Access
The hereditary spastic paraplegias
John K. Fink
Elsevier eBooks (2024), pp. 183-212
Closed Access
Cell type–specific gene therapy confers protection against motor neuron disease caused by a TFG variant
Molly M. Lettman, Caitlin A. Mendina, Emma Burkard, et al.
Proceedings of the National Academy of Sciences (2024) Vol. 121, Iss. 47
Closed Access
Oligodendrocytes, the Forgotten Target of Gene Therapy
Yasemin Güneş, Catherine Le Stunff, Pierre Bougnères
Cells (2024) Vol. 13, Iss. 23, pp. 1973-1973
Open Access
Intrathecal delivery of a bicistronic AAV9 vector expressing β-hexosaminidase A corrects Sandhoff disease in a murine model: A dosage study
Alex E. Ryckman, Natalie M. Deschenes, Brianna M. Quinville, et al.
Molecular Therapy — Methods & Clinical Development (2023) Vol. 32, Iss. 1, pp. 101168-101168
Open Access | Times Cited: 1
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