
OpenAlex is a bibliographic catalogue of scientific papers, authors and institutions accessible in open access mode, named after the Library of Alexandria. It's citation coverage is excellent and I hope you will find utility in this listing of citing articles!
If you click the article title, you'll navigate to the article, as listed in CrossRef. If you click the Open Access links, you'll navigate to the "best Open Access location". Clicking the citation count will open this listing for that article. Lastly at the bottom of the page, you'll find basic pagination options.
Requested Article:
Intrathecal/Intracerebroventricular enzyme replacement therapy for the mucopolysaccharidoses: efficacy, safety, and prospects
Roberto Giugliani, Amauri Dalla Corte, Fabiano de Oliveira Poswar, et al.
Expert Opinion on Orphan Drugs (2018) Vol. 6, Iss. 7, pp. 403-411
Closed Access | Times Cited: 13
Roberto Giugliani, Amauri Dalla Corte, Fabiano de Oliveira Poswar, et al.
Expert Opinion on Orphan Drugs (2018) Vol. 6, Iss. 7, pp. 403-411
Closed Access | Times Cited: 13
Showing 13 citing articles:
Mucopolysaccharidosis Type II: One Hundred Years of Research, Diagnosis, and Treatment
Francesca D’Avanzo, Laura Rigon, Alessandra Zanetti, et al.
International Journal of Molecular Sciences (2020) Vol. 21, Iss. 4, pp. 1258-1258
Open Access | Times Cited: 121
Francesca D’Avanzo, Laura Rigon, Alessandra Zanetti, et al.
International Journal of Molecular Sciences (2020) Vol. 21, Iss. 4, pp. 1258-1258
Open Access | Times Cited: 121
Therapeutic Options for Mucopolysaccharidoses: Current and Emerging Treatments
Kazuki Sawamoto, Molly Stapleton, Carlos Javier Alméciga-Díaz, et al.
Drugs (2019) Vol. 79, Iss. 10, pp. 1103-1134
Closed Access | Times Cited: 77
Kazuki Sawamoto, Molly Stapleton, Carlos Javier Alméciga-Díaz, et al.
Drugs (2019) Vol. 79, Iss. 10, pp. 1103-1134
Closed Access | Times Cited: 77
Enzyme replacement therapy for mucopolysaccharidoses; past, present, and future
Hui Hsuan Chen, Kazuki Sawamoto, Robert W. Mason, et al.
Journal of Human Genetics (2019) Vol. 64, Iss. 11, pp. 1153-1171
Closed Access | Times Cited: 55
Hui Hsuan Chen, Kazuki Sawamoto, Robert W. Mason, et al.
Journal of Human Genetics (2019) Vol. 64, Iss. 11, pp. 1153-1171
Closed Access | Times Cited: 55
Mucopolysaccharidosis Type I: Current Treatments, Limitations, and Prospects for Improvement
Christiane S. Hampe, Jacob Wesley, Troy C. Lund, et al.
Biomolecules (2021) Vol. 11, Iss. 2, pp. 189-189
Open Access | Times Cited: 55
Christiane S. Hampe, Jacob Wesley, Troy C. Lund, et al.
Biomolecules (2021) Vol. 11, Iss. 2, pp. 189-189
Open Access | Times Cited: 55
Differences in MPS I and MPS II Disease Manifestations
Christiane S. Hampe, Brianna Yund, Paul J. Orchard, et al.
International Journal of Molecular Sciences (2021) Vol. 22, Iss. 15, pp. 7888-7888
Open Access | Times Cited: 32
Christiane S. Hampe, Brianna Yund, Paul J. Orchard, et al.
International Journal of Molecular Sciences (2021) Vol. 22, Iss. 15, pp. 7888-7888
Open Access | Times Cited: 32
Targeted enzyme delivery systems in lysosomal disorders: an innovative form of therapy for mucopolysaccharidosis
Azam Safary, Mostafa Akbarzadeh-Khiavi, Yadollah Omidi, et al.
Cellular and Molecular Life Sciences (2019) Vol. 76, Iss. 17, pp. 3363-3381
Open Access | Times Cited: 23
Azam Safary, Mostafa Akbarzadeh-Khiavi, Yadollah Omidi, et al.
Cellular and Molecular Life Sciences (2019) Vol. 76, Iss. 17, pp. 3363-3381
Open Access | Times Cited: 23
Precision Medicine for Lysosomal Disorders
Filippo Pinto e Vairo, Diana Rojas Málaga, Francyne Kubaski, et al.
Biomolecules (2020) Vol. 10, Iss. 8, pp. 1110-1110
Open Access | Times Cited: 21
Filippo Pinto e Vairo, Diana Rojas Málaga, Francyne Kubaski, et al.
Biomolecules (2020) Vol. 10, Iss. 8, pp. 1110-1110
Open Access | Times Cited: 21
Fetal therapies and trials for lysosomal storage diseases: a survey of attitudes of parents and patients
Marisa E. Schwab, Julia E. H. Brown, Billie R. Lianoglou, et al.
Orphanet Journal of Rare Diseases (2022) Vol. 17, Iss. 1
Open Access | Times Cited: 13
Marisa E. Schwab, Julia E. H. Brown, Billie R. Lianoglou, et al.
Orphanet Journal of Rare Diseases (2022) Vol. 17, Iss. 1
Open Access | Times Cited: 13
The Interplay of Glycosaminoglycans and Cysteine Cathepsins in Mucopolysaccharidosis
Alexis David, Thibault Chazeirat, Ahlame Saidi, et al.
Biomedicines (2023) Vol. 11, Iss. 3, pp. 810-810
Open Access | Times Cited: 6
Alexis David, Thibault Chazeirat, Ahlame Saidi, et al.
Biomedicines (2023) Vol. 11, Iss. 3, pp. 810-810
Open Access | Times Cited: 6
Carbohydrate‐Based Therapeutics for Lysosomal Storage Disorders
Camilla Matassini, Francesca Clemente, Francesca Cardona
(2023), pp. 245-292
Closed Access | Times Cited: 2
Camilla Matassini, Francesca Clemente, Francesca Cardona
(2023), pp. 245-292
Closed Access | Times Cited: 2
Therapeutic Options for Mucopolysaccharidosis II (Hunter Disease)
Francyne Kubaski, Filippo Pinto e Vairo, Guilherme Baldo, et al.
Current Pharmaceutical Design (2020) Vol. 26, Iss. 40, pp. 5100-5109
Closed Access | Times Cited: 5
Francyne Kubaski, Filippo Pinto e Vairo, Guilherme Baldo, et al.
Current Pharmaceutical Design (2020) Vol. 26, Iss. 40, pp. 5100-5109
Closed Access | Times Cited: 5
Characterization of a HIR-Fab-IDS, Novel Iduronate 2-Sulfatase Fusion Protein for the Treatment of Neuropathic Mucopolysaccharidosis Type II (Hunter Syndrome)
В. Д. Гусарова, Maksim Smolov, I. V. Lyagoskin, et al.
BioDrugs (2023) Vol. 37, Iss. 3, pp. 375-395
Closed Access | Times Cited: 1
В. Д. Гусарова, Maksim Smolov, I. V. Lyagoskin, et al.
BioDrugs (2023) Vol. 37, Iss. 3, pp. 375-395
Closed Access | Times Cited: 1
Current Approaches to the Treatment of Hunter Syndrome
Ekaterina Zakharova, Elena Voskoboeva, А. N. Semyachkina, et al.
Педиатрическая фармакология (2018) Vol. 15, Iss. 4, pp. 324-332
Open Access | Times Cited: 1
Ekaterina Zakharova, Elena Voskoboeva, А. N. Semyachkina, et al.
Педиатрическая фармакология (2018) Vol. 15, Iss. 4, pp. 324-332
Open Access | Times Cited: 1